North Star Assessment for limb-girdle type muscular dystrophies (NSAD)

June 04,2024

Download scientific diagram | North Star Assessment for limb-girdle type muscular dystrophies (NSAD) person-item threshold distribution plot demonstrating good coverage of items for the population. The top histogram illustrates the abilities of the population, from the weakest on the left to the strongest on the right. The bottom histogram demonstrates a well-distributed range of items that test the ability of the population, with a ceiling for the individuals who were the very strongest and asymptomatic. from publication: Validation of the North Star Assessment for Limb-Girdle Type Muscular Dystrophies | Objective. The North Star Assessment for limb-girdle type muscular dystrophies (NSAD), a clinician-reported outcome measure (ClinRO) of motor performance, was initially developed and validated for use in dysferlinopathy, an autosomal recessive form of limb-girdle muscular | Muscular Dystrophy, Limb-Girdle Muscular Dystrophies and Neuromuscular Diseases | ResearchGate, the professional network for scientists.

North Star Assessment for limb-girdle type muscular dystrophies (NSAD)

SEC Filing Sarepta Therapeutics, Inc.

Association between Total NSAD score and ACTIVLIM. NSAD, North Star

IJMS, Free Full-Text

LGMD2E Children Show Benefits of SRP-9003 Gene Therapy After 1 Year

Limb-girdle muscular dystrophies — international collaborations for translational research

Muscular Dystrophy Association Singapore - Today is Limb-Girdle Muscular Dystrophy (LGMD) Awareness Day! Limb-girdle muscular dystrophies (LGMD) are a rare group of progressive genetic illnesses that usually affects the proximal muscles around

IJMS, Free Full-Text

Miyoshi myopathy and limb girdle muscular dystrophy R2 are the same disease - ScienceDirect